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Advancements in MPS I Treatment: 4 Breakthrough Therapies on the Horizon | #mucopolysaccharidosis type i market # aldurazyme patent expiration # mucopolysaccharidosis i clinical trials market # mps pipeline # hurler scheie syndrome market forcast # hurler scheie syndrome market # sanofi mucopolysaccharidosis / mps i # isp therapies

Advancements in MPS I Treatment: 4 Breakthrough Therapies on the Horizon

Advancements in MPS I Treatment: 4 Breakthrough Therapies on the Horizon

Mucopolysaccharidosis Type I (MPS I) is a rare genetic disorder that disrupts the body's ability to break down glycosaminoglycans (GAGs), leading to severe organ and tissue damage. While traditional treatments like enzyme replacement therapy (ERT) have provided significant benefits,